| Product Code: ETC8833717 | Publication Date: Sep 2024 | Updated Date: Sep 2025 | Product Type: Market Research Report | |
| Publisher: 6Wresearch | Author: Bhawna Singh | No. of Pages: 75 | No. of Figures: 35 | No. of Tables: 20 |
This market includes treatments for rare blood disorders like hemophilia and paroxysmal nocturnal hemoglobinuria. Growth is slow but supported by government rare disease frameworks, NGO efforts, and improving diagnostic capabilities in specialized healthcare facilities.
The acquired orphan blood diseases therapeutics market is estimated to reach USD 12.0 billion by 2033, growing at a CAGR of 7.5% from 2026 to 2033 . In the Philippines, the market is expected to expand due to increasing prevalence of rare blood disorders and advancements in therapeutic options.
Therapeutics for orphan blood diseases face challenges including high R&D costs and limited local clinical trials. The small patient population reduces market incentives for pharmaceutical companies. Additionally, regulatory hurdles and reimbursement issues limit availability.
Orphan blood diseases often lack sufficient treatment options, opening opportunities for pharmaceutical companies specializing in rare disease drugs. Investments can focus on developing supply chains, raising awareness, and supporting healthcare providers with training and resources to manage these conditions effectively.
Orphan diseases, including rare blood disorders, receive policy attention through the Rare Diseases Act and the DOHâs Rare Disease Program. These policies provide frameworks for patient registration, access to orphan drugs, and support for research and local drug development. The government also emphasizes equitable healthcare access through PhilHealth coverage expansions for orphan therapeutics.
1 Executive Summary |
2 Introduction |
2.1 Key Highlights of the Report |
2.2 Report Description |
2.3 Market Scope & Segmentation |
2.4 Research Methodology |
2.5 Assumptions |
3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Overview |
3.1 Philippines Country Macro Economic Indicators |
3.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, 2021 & 2031F |
3.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market - Industry Life Cycle |
3.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market - Porter's Five Forces |
3.5 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume Share, By Diagnosis, 2021 & 2031F |
3.6 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume Share, By Symptoms, 2021 & 2031F |
3.7 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume Share, By DistributionChannels, 2021 & 2031F |
3.8 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume Share, By Therapies Covered, 2021 & 2031F |
4 Philippines Acquired Orphan Blood Diseases Therapeutics Market Dynamics |
4.1 Impact Analysis |
4.2 Market Drivers |
4.2.1 Increasing prevalence of acquired orphan blood diseases in the Philippines |
4.2.2 Growing awareness and diagnosis of rare blood disorders |
4.2.3 Advancements in therapeutic options for orphan blood diseases |
4.3 Market Restraints |
4.3.1 Limited accessibility and affordability of specialized treatments |
4.3.2 Regulatory challenges in drug approval for rare diseases |
4.3.3 Lack of skilled healthcare professionals in managing orphan blood diseases |
5 Philippines Acquired Orphan Blood Diseases Therapeutics Market Trends |
6 Philippines Acquired Orphan Blood Diseases Therapeutics Market, By Types |
6.1 Philippines Acquired Orphan Blood Diseases Therapeutics Market, By Diagnosis |
6.1.1 Overview and Analysis |
6.1.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Diagnosis, 2021- 2031F |
6.1.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Recombinantfactor, 2021- 2031F |
6.1.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Immuno globulin infusion therapy, 2021- 2031F |
6.1.5 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Activated prothrombin complex concentrate, 2021- 2031F |
6.1.6 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Thrombopoietin receptor agonists, 2021- 2031F |
6.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market, By Symptoms |
6.2.1 Overview and Analysis |
6.2.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Agranulocytosis, 2021- 2031F |
6.2.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Hemophilia, 2021- 2031F |
6.2.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Von Willebrand Syndrome, 2021- 2031F |
6.2.5 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Paroxysmal Nocturnal Hemoglobinuria, 2021- 2031F |
6.2.6 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Myelodysplastic Syndrome, 2021- 2031F |
6.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market, By DistributionChannels |
6.3.1 Overview and Analysis |
6.3.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Hospital Pharmacy, 2021- 2031F |
6.3.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Retail Pharmacy, 2021- 2031F |
6.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market, By Therapies Covered |
6.4.1 Overview and Analysis |
6.4.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Recombinant Factor, 2021- 2031F |
6.4.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Immunoglobulin Infusion Therapy, 2021- 2031F |
6.4.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Activated Prothrombin Complex Concentrate, 2021- 2031F |
6.4.5 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenues & Volume, By Thrombopoietin Receptor Agonists, 2021- 2031F |
7 Philippines Acquired Orphan Blood Diseases Therapeutics Market Import-Export Trade Statistics |
7.1 Philippines Acquired Orphan Blood Diseases Therapeutics Market Export to Major Countries |
7.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Imports from Major Countries |
8 Philippines Acquired Orphan Blood Diseases Therapeutics Market Key Performance Indicators |
8.1 Patient enrollment in clinical trials for orphan blood disease therapies |
8.2 Adoption rate of new treatments for acquired orphan blood diseases |
8.3 Number of research collaborations and partnerships focused on orphan blood diseases |
8.4 Rate of healthcare provider training programs on managing rare blood disorders |
8.5 Patient satisfaction and quality of life improvements with orphan blood disease treatments. |
9 Philippines Acquired Orphan Blood Diseases Therapeutics Market - Opportunity Assessment |
9.1 Philippines Acquired Orphan Blood Diseases Therapeutics Market Opportunity Assessment, By Diagnosis, 2021 & 2031F |
9.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Opportunity Assessment, By Symptoms, 2021 & 2031F |
9.3 Philippines Acquired Orphan Blood Diseases Therapeutics Market Opportunity Assessment, By DistributionChannels, 2021 & 2031F |
9.4 Philippines Acquired Orphan Blood Diseases Therapeutics Market Opportunity Assessment, By Therapies Covered, 2021 & 2031F |
10 Philippines Acquired Orphan Blood Diseases Therapeutics Market - Competitive Landscape |
10.1 Philippines Acquired Orphan Blood Diseases Therapeutics Market Revenue Share, By Companies, 2024 |
10.2 Philippines Acquired Orphan Blood Diseases Therapeutics Market Competitive Benchmarking, By Operating and Technical Parameters |
11 Company Profiles |
12 Recommendations |
13 Disclaimer |